World’s first patient treated with personalized CRISPR gene editing therapy
Landmark study showcases the power of personalized CRISPR gene editing therapy to treat a patient with rare metabolic disease. …
COVID-19 vaccine reduces long COVID in children
COVID-19 vaccination was associated with moderate protection against long COVID in large, diverse cohort of children. …
Climate change may lead to increase in kidney stones
Modeling study suggests rising temperatures due to climate change will lead to an increase in cases of kidney stones over the next seven decades. …
Novel gene therapy for hemophilia a leads to sustained expression of clotting factor and reduced bleeding events
Novel gene therapy for hemophilia A led to sustained expression of clotting factor VIII, resulting in reduction or complete elimination of potentially life-threatening bleeding events.
Researchers reverse severe lymphatic disorder in patient with Noonan syndrome
Precise treatment of a lymphatic disorder leads to resolution of patient’s debilitating symptoms and complete remodeling of her lymphatic system. …
Genomic study reveals role for hypothalamus in inflammatory bowel disease
Integrating 3D genomics with genome-wide genetic data, researchers uncovered genetic correlations between inflammatory bowel disease, stress, and depression. …
Severe lymphatic disorder effectively treated with precision medicine
Treatment of a severe lymphatic disorder that targeted a mutation in a well-studied genetic pathway led to the complete resolution of symptoms and remodeling of the lymphatic system. …
Transplanting gut bacteria alters depression-related behavior, brain inflammation in animals
Scientists have shown that transplanting gut bacteria, from an animal that is vulnerable to social stress to a non-stressed animal, can cause vulnerable behavior in the recipient. …
Guided by CRISPR, prenatal gene editing shows proof-of-concept in treating disease before birth
For the first time, scientists have performed prenatal gene editing to prevent a lethal metabolic disorder in laboratory animals, offering the potential to treat human congenital diseases before birth. …
Babies fed soy-based formula have changes in reproductive system tissues
Infants who consumed soy-based formula as newborns had differences in some reproductive-system cells and tissues, compared to those who used cow-milk formula or were breastfed, according to a new study. …
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